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TRANSGENIC MOUSE LACKING ENDOGENOUS FVIII AND VWF - A MODEL OF HEMOPHILIA A
TRANSGENIC MOUSE LACKING ENDOGENOUS FVIII AND VWF - A MODEL OF HEMOPHILIA A
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机译:缺乏内源性FVIII和VWF的转基因小鼠-血友病A模型。
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摘要
The present invention relates, generally, to a transgenic non-human animal model of hemophilia A, wherein the transgenic animal is deficient in endogenous Factor VIII and endogenous von Willebrand Factor, and methods to treat hereditary or acquired hemophilia A or von Willebrand Disease (VWD) by administration of exogenous human VWF.
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