首页> 美国卫生研究院文献>Springer Open Choice >An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical Trials

【2h】

An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical Trials

机译：Nusinersen治疗的婴儿和儿童症状性脊髓性肌萎缩症（SMA）的综合安全性分析在七个临床试验中。

代理获取

本网站仅为用户提供外文OA文献查询和代理获取服务，本网站没有原文。下单后我们将采用程序或人工为您竭诚获取高质量的原文，但由于OA文献来源多样且变更频繁，仍可能出现获取不到、文献不完整或与标题不符等情况，如果获取不到我们将提供退款服务。请知悉。

页面导航

摘要
著录项
引文网络
相似文献
相关主题

摘要

BackgroundTreatment with nusinersen has demonstrated significant and clinically meaningful benefits in clinical trials in infants and children with spinal muscular atrophy (SMA).

机译：背景在新生儿和脊髓性肌萎缩症（SMA）的儿童临床试验中，使用Nusinersen进行治疗已显示出显着且具有临床意义的益处。

著录项

期刊名称 Springer Open Choice
作者
Basil T. Darras; Michelle A. Farrar; Eugenio Mercuri; Richard S. Finkel; Richard Foster; Steven G. Hughes; Ishir Bhan; Wildon Farwell; Sarah Gheuens;
展开▼
作者单位

展开▼
年(卷),期 -1(33),9
年度 -1
页码 919–932
总页数 14
原文格式 PDF
正文语种
中图分类外科学;
关键词

相似文献

外文文献
中文文献
专利

1. An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical Trials [J] . Darras Basil T., Farrar Michelle A., Mercuri Eugenio, CNS drugs . 2019,第9期

机译：七次临床试验中植株血肌萎缩（SMA）对症状脊髓肌萎缩（SMA）的综合安全分析
2. Infants and children with SMA treated with nusinersen in clinical trials: an integrated safety analysis [J] . Mercuri E., Finkel R., Farrar M., Neuromuscular disorders: NMD . 2017,第Suppla2期

机译：患有培养的婴儿和儿童在临床试验中治疗NUSINSEN：综合安全分析
3. Infants and children with SMA treated with nusinersen in clinical trials: an integrated safety analysis [J] . Mercuri E., Finkel R., Farrar M., Neuromuscular disorders: NMD . 2017,第Suppla2期

机译：患有培养的婴儿和儿童在临床试验中治疗NUSINSEN：综合安全分析
4. RESULT OF CLINICAL TRIALS WITH CHILDREN WITH SPINAL MUSCULAR ATROPHY USING THE ATLAS 2020 LOWER-LIMB ACTIVE ORTHOSIS [C] . DANIEL SANZ-MERODIO, MANUEL PEREZ, MANUEL PRIETO, International Conference on Climbing and Walking Robots and the Support Technologies for Mobile Machines . 2018

机译：使用ATLAS 2020下肢活性矫形器与脊柱肌萎缩儿童临床试验的结果
5. Nusinersen Treatment and Healthcare Costs in Spinal Muscular Atrophy [D] . Fox, David A. 2020

机译：血缘肌肉萎缩的螺母治疗和医疗保健成本
6. Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study [O] . Darryl C. De Vivo, Enrico Bertini, Kathryn J. Swoboda, -1

机译：Nusinersen在症状性脊髓性肌萎缩症的症状前期开始于婴儿：2期NURTURE研究的中期疗效和安全性结果
7. An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical Trials [O] . Basil T. Darras, Michelle A. Farrar, Eugenio Mercuri, 2019

机译：七次临床试验中植株血肌萎缩（SMA）对症状脊髓肌萎缩（SMA）的综合安全分析
8. Columbia SMA Project: A Randomized, Control Trial of the Effects of Exercise on Motor Function and Strength in Patients with Spinal Muscular Atrophy (SMA). [R] . De Vivo, D. C. 2012

机译：哥伦比亚sma项目：运动对脊髓性肌萎缩症（sma）患者运动功能和力量影响的随机对照试验。

An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical Trials

摘要

著录项

引文网络

相似文献

相关主题

期刊订阅