机译:脊髓性肌肉萎缩的SMNΔ7模型中的早期心力衰竭,并通过产后scAAV9-SMN递送进行纠正
Department of Gene Therapy, The Research Institute and|Integrated Biomedical Sciences Graduate Program and;
The Center for Cardiovascular and Pulmonary Research and The Heart Center, Nationwide Children's Hospital, Columbus, OH 43205, USA,|Department of Pharmacology and Experimental Therapeutics, Louisiana State University Health Sciences Center, New Orleans, LA, USA,;
Department of Gene Therapy, The Research Institute and;
Department of Gene Therapy, The Research Institute and;
Department of Molecular and Cellular Biochemistry, The Ohio State University, Columbus, OH 43210, USA,;
Department of Gene Therapy, The Research Institute and;
Specialty VETPATH, Seattle, WA 98103, USA,;
Department of Anatomical Sciences & Neurobiology and|Kentucky Spinal Cord Injury Research Center, Department of Neurological Surgery, University of Louisville, Louisville, KY 40292, USA;
The Center for Cardiovascular and Pulmonary Research and The Heart Center, Nationwide Children's Hospital, Columbus, OH 43205, USA,;
Integrated Biomedical Sciences Graduate Program and|Department of Molecular and Cellular Biochemistry, The Ohio State University, Columbus, OH 43210, USA,;
机译:脊髓性肌萎缩的SMNDelta7模型中的早期心力衰竭,以及通过产后scAAV9-SMN递送进行纠正。
机译:有症状的Smn-/-; SMN2 ++脊髓性肌萎缩症小鼠在scAAV9-SMN递送后降低疾病严重程度
机译:出生后早期SMN传递对小鼠模型中脊髓性肌萎缩表型的拯救
机译:计算建模方法,建议对脊髓性肌萎缩症进行可能的治疗干预
机译:曲古抑菌素A对脊髓性肌萎缩症的中级小鼠模型的Smn依赖性有益作用。
机译:脊髓性肌肉萎缩的SMNΔ7模型中的早期心力衰竭并通过产后scAAV9-SMN递送进行纠正
机译:脊髓性肌肉萎缩的SMNΔ7模型中的早期心力衰竭,并通过产后scAAV9-SMN递送进行纠正