首页> 外国专利> TREATMENT OF RNASE H1 RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO RNASE H1

TREATMENT OF RNASE H1 RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO RNASE H1

机译:通过抑制天然抗转录酶对RNASE H1的治疗RNASE H1相关疾病

摘要

The present invention relates to antisense oligonucleotides that modulate the expression of and/or function of RNase H1, in particular, by targeting natural antisense polynucleotides of RNase H1. The invention also relates to the identification of these antisense oligonucleotides and their use in treating diseases and disorders associated with the expression of RNASE H1.
机译:本发明涉及反义寡核苷酸,其特别是通过靶向RNase H1的天然反义多核苷酸来调节RNase H1的表达和/或功能。本发明还涉及这些反义寡核苷酸的鉴定及其在治疗与RNASE H1表达有关的疾病和病症中的用途。

著录项

  • 公开/公告号EP2529015B1

    专利类型

  • 公开/公告日2017-11-15

    原文格式PDF

  • 申请/专利权人 CURNA INC.;

    申请/专利号EP20110735332

  • 发明设计人 COLLARD JOSEPH;KHORKOVA SHERMAN OLGA;

    申请日2011-01-25

  • 分类号C12N15/113;A61K31/7088;A61K48;C12N15/63;C12N9/22;

  • 国家 EP

  • 入库时间 2022-08-21 13:18:29

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