首页> 外国专利> FXN FXN TREATMENT OF FRATAXIN FXN RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO FXN

FXN FXN TREATMENT OF FRATAXIN FXN RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO FXN

机译:FXN FXN抑制自然抗转录酶对FXN的治疗与法拉辛FXN相关疾病

摘要

The present invention particularly relates to antisense oligonucleotides that modulate expression and / or function of prataxin (FXN) by targeting natural antisense polynucleotides of prataxin (FXN). The invention also relates to their use in the treatment of diseases and disorders associated with the identification of these antisense oligonucleotides and the expression of prataxin (FXN).
机译:本发明特别涉及通过靶向天然的prataxin(FXN)反义多核苷酸来调节prataxin(FXN)的表达和/或功能的反义寡核苷酸。本发明还涉及它们在治疗与这些反义寡核苷酸的鉴定和prataxin(FXN)的表达有关的疾病和病症中的用途。

著录项

  • 公开/公告号KR102043422B1

    专利类型

  • 公开/公告日2019-11-11

    原文格式PDF

  • 申请/专利权人

    申请/专利号KR20137034424

  • 申请日2012-06-08

  • 分类号C12N15/113;A61K48;

  • 国家 KR

  • 入库时间 2022-08-21 11:08:31

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