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机译:具有基因转移的GSDIII表型的拯救需要肝脏和肌肉靶向GDE表达
INTEGRARE Genethon Inserm;
Dino Ferrari Centre Neuroscience Section Department of Pathophysiology and Transplantation (DEPT;
INTEGRARE Genethon Inserm;
INTEGRARE Genethon Inserm;
INTEGRARE Genethon Inserm;
Université Lyon 1;
INTEGRARE Genethon Inserm;
University Pierre and Marie Curie Paris 6 and INSERM U974;
INTEGRARE Genethon Inserm;
INTEGRARE Genethon Inserm;
INTEGRARE Genethon Inserm;
Dino Ferrari Centre Neuroscience Section Department of Pathophysiology and Transplantation (DEPT;
Genethon;
Genethon;
Genethon;
INTEGRARE Genethon Inserm;
Myology Institute Neuromuscular Morphology Unit Groupe Hospitalier Universitaire La Pitié-Salp;
Myology Institute Neuromuscular Morphology Unit Groupe Hospitalier Universitaire La Pitié-Salp;
Université Lyon 1;
Université Lyon 1;
Dino Ferrari Centre Neuroscience Section Department of Pathophysiology and Transplantation (DEPT;
INTEGRARE Genethon Inserm;
INTEGRARE Genethon Inserm;
glycogen storage disease type III; neuromuscular disease; adeno-associated vector; glycogenosis; Cori disease; gene therapy; dual AAV vectors; acid-alpha-glucosidase;
机译:具有基因转移的GSDIII表型的拯救需要肝脏和肌肉靶向GDE表达
机译:基因转移救出了Rett综合征小鼠模型中的成立表型
机译:rAAV介导的截短的CFTR的基因转移抢救人肠道有机体和CF小鼠中的囊性纤维化表型
机译:在小鼠体内将裸质粒DNA分配到肝表面后,肝和叶选择性基因的表达
机译:合作致癌突变诱导的自噬对于癌症表型是必不可少的,并且需要表达新的合作反应基因Plac8
机译:通过基因转移挽救GSDIII表型需要肝和肌肉靶向的GDE表达
机译:具有基因转移的GSDIII表型的拯救需要肝脏和肌肉靶向GDE表达