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机译:来自脑病理学的N-乙酰己二酸盐:对Canavan病因基因治疗的影响
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Mark Wainwright Analyt Ctr Biomed Imaging Resources Lab Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
UNSW Sydney Mark Wainwright Analyt Ctr Bioanalyt Mass Spectrometry Facil Sydney NSW 2052;
UNSW Sydney Mark Wainwright Analyt Ctr Transgen Anim Unit Sydney NSW 2052 Australia;
Neurosci Res Australia Barker St Randwick NSW 2031 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
Alfred Hosp Dept Anat Pathol Melbourne Vic Australia;
UNSW Australia Prince Wales Clin Sch Level 2 C25 Lowy Bldg Sydney NSW 2052 Australia;
Heidelberg Univ Med Fac Mannheim Cent Inst Mental Hlth Inst Psychopharmacol D-68159 Mannheim;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
Neurosci Res Australia Barker St Randwick NSW 2031 Australia;
UNSW Sydney Sch Med Sci Translat Neurosci Facil Sydney NSW 2052 Australia;
N-Acetylaspartate; Canavan disease; Myelination; White matter disorder; Brain metabolism; Neurophysiology; AAV; Gene therapy;
机译:来自脑病理学的N-乙酰己二酸盐:对Canavan病因基因治疗的影响
机译:Canavan病的醋酸补充疗法的进展:甘油三乙酸酯的管理增加了脑中醋酸盐的水平,但不增加N-乙酰乙酰天冬氨酸的水平
机译:缺陷的N-乙酰天门冬氨酸分解代谢降低了Canavan's病的大脑乙酸盐水平和髓磷脂合成
机译:用于治疗神经退行性脑病的光致调节治疗条件分析
机译:脑切片中错折叠蛋白神经毒性的前体内建模:对慢性神经变性疾病的机械和翻译发现的影响
机译:N-乙酰天门冬氨酸与脑病理学脱钩:对Canavan疾病基因治疗的意义
机译:在出生后髓鞘形成期间增加脑中的N-乙酰天冬氨酸不会导致Canavan病的CNs病理