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机译:IVA型粘多糖贮积病(Morquio A病):临床评价和当前治疗方法:特别评价
The Department of Pediatrics,Saint Louis University, Doisy Research Center Room 307, 1100 South Grand Blvd., St. Louis, MO 63104., USA;
Department of Pediatrics, Saint Louis University, St. Louis, MO, USA;
Department of Pediatrics, Saint Louis University, St. Louis, MO, USA;
Department of Pediatrics, Saint Louis University, St. Louis, MO, USA;
International Morquio Organization, Phoenix,AZ, USA;
Institute for the Study of Inborn Errors of Metabolism, Pontificia Universidad Javeriana, Bogota D.C., Colombia;
Department of Pediatrics, Faculty of Medicine University of the Ryukyus, Okinawa, Japan;
Alfred I. duPont Hospital for Children, Wilmington, DL;
Alfred I. duPont Hospital for Children, Wilmington, DL;
Department of Pediatrics, Gifu University, Gifu, Japan;
Department of Pediatrics, Gifu University, Gifu, Japan;
mucopolysaccharidosis IVA; keratan sulfate; GALNS; chondrodysplasia; enzyme replacement therapy; bone marrow transplantation; tandem mass spectrometry.;
机译:Elosulfase Alfa:在IVA型粘多糖贮积病(Morquio A综合征)患者中的应用综述
机译:马来西亚IVA(Morquio A综合征)粘多糖贮积病患者的临床,生化和遗传学特征:首次国家自然历史队列研究
机译:马来西亚IVA(Morquio A综合征)粘多糖贮积病患者的临床,生化和遗传学特征:首次国家自然历史队列研究
机译:Azilsartan Medoxomil临床药代动力学治疗心血管疾病:综述
机译:神经反馈治疗多动症:当前证据和临床试验的系统评价
机译:马来西亚IVA(Morquio A综合征)粘多糖贮积病患者的临床生化和遗传学特征:首次国家自然历史队列研究
机译:儿童伴随粘多糖尿病IVA和神经源性膀胱型临床和遗传特征:两种报告与文献综述