Treatment of Fabry disease in ERT naive and ERT-experienced patients

摘要

PROBLEM TO BE SOLVED: To provide a dosing regimen for treating Fabry disease of a patient. SOLUTION: The treatment of an ERT-experienced Fabry disease patient or an ERT naive (untreated) Fabry disease patient is provided. Certain methods include administering to a patient about 123 mg of a free base equivalent of Miguel Rastat to improve left ventricular weight and / or to improve podocyte globotriosylceramide. [Selection diagram] Fig. 3