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MEDICINE FOR GENETIC TREATMENT OF DILATED CARDIOMYOPATHY
MEDICINE FOR GENETIC TREATMENT OF DILATED CARDIOMYOPATHY
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机译:遗传性扩张性心肌病的治疗药物
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摘要
PROBLEM TO BE SOLVED: To construct a gene expression vector that can be used for genetically treating a patient suffering from dilated cardiomyopathy. SOLUTION: This is a gene expression vector obtained by integrating a gene encoding sarcoglycan into an adeno-associated virus(AAV) vector.
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