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COMPOSITIONS AND METHODS FOR IDENTIFYING, MODULATING AND MONITORING DRUG TARGETS IN MUSCULAR DISEASE

机译:鉴定,调节和监测肌​​肉疾病中药物靶标的组合物和方法

摘要

The present disclosure relates to customized therapy for disease. The present disclosure also relates to aptamer-based compositions and methods for identifying, modulating and monitoring drug targets in muscular disease (e.g., Duchenne muscular dystrophy).
机译:本公开涉及针对疾病的定制疗法。本公开还涉及用于鉴定,调节和监测肌​​肉疾病(例如,杜兴氏肌营养不良症)中的药物靶标的基于适体的组合物和方法。

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