机译:通过体内递送基因组编辑剂治疗常染色体显性遗传性听力损失
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA|Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA|Broad Inst MIT & Harvard, Cambridge, MA 02141 USA|Rice Univ, Dept Chem & Biomol Engn, Houston, TX 77005 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA|Huazhong Univ Sci & Technol, Tongji Med Coll, Union Hosp, Dept Otorhinolaryngol, Wuhan 430022, Hubei, Peoples R China|Shanghai Jiao Tong Univ, Sch Med, Peoples Hosp 9, Dept Otolaryngol Head & Neck Surg, Shanghai 200011, Peoples R China|Shanghai Jiao Tong Univ, Sch Med, Ear Inst, Shanghai 200011, Peoples R China;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA;
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA|Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA|Broad Inst MIT & Harvard, Cambridge, MA 02141 USA|Harvard Univ, Program Speech & Hearing Biosci & Technol, Cambridge, MA 02138 USA;
Boston Childrens Hosp, FM Kirby Neurobiol Ctr, Dept Otolaryngol, Boston, MA 02115 USA|Boston Childrens Hosp, FM Kirby Neurobiol Ctr, Dept Neurol, Boston, MA 02115 USA|Harvard Med Sch, Boston, MA 02115 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA|Huazhong Univ Sci & Technol, Tongji Med Coll, Union Hosp, Dept Otorhinolaryngol, Wuhan 430022, Hubei, Peoples R China;
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA|Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA|Broad Inst MIT & Harvard, Cambridge, MA 02141 USA;
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA|Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA|Fudan Univ, Shanghai Med Coll, Eye & ENT Hosp, Dept Otolaryngol Head & Neck Surg, Shanghai, Peoples R China;
Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA|Chinese PLA Med Sch, Key Lab Hearing Impairment Prevent & Treatment Be, Minist Educ, Dept Otolaryngol & Head Neck Surg,Key Lab Hearing, Beijing, Peoples R China;
Chinese PLA Med Sch, Key Lab Hearing Impairment Prevent & Treatment Be, Minist Educ, Dept Otolaryngol & Head Neck Surg,Key Lab Hearing, Beijing, Peoples R China;
Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA;
Huazhong Univ Sci & Technol, Tongji Med Coll, Union Hosp, Dept Otorhinolaryngol, Wuhan 430022, Hubei, Peoples R China;
Boston Childrens Hosp, FM Kirby Neurobiol Ctr, Dept Otolaryngol, Boston, MA 02115 USA|Boston Childrens Hosp, FM Kirby Neurobiol Ctr, Dept Neurol, Boston, MA 02115 USA|Harvard Med Sch, Boston, MA 02115 USA;
Harvard Med Sch, Dept Otolaryngol & Program Neurosci, Boston, MA 02114 USA|Massachusetts Eye & Ear Infirm, Eaton Peabody Lab, Boston, MA 02114 USA;
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA|Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA|Broad Inst MIT & Harvard, Cambridge, MA 02141 USA;
机译:渐进式显性听力损失(常染色体显性耳聋-41)和P2RX2 P2RX2基因突变:一种表型 - 基因型研究
机译:CRISPR / CAS9:针对治疗遗传性听力损失的靶向基因组编辑
机译:i- GONAD(通过输卵管核酸传递改善的基因组编辑),一种方便的体内工具,可产生经基因组编辑的大鼠
机译:技术变革的社会主体:新兴技术的含义,期望和情感的动态和差异:基因组编辑的案例
机译:在17q25上绘制一个新的常染色体显性遗传性听力损失基因座DFNA20,并寻找引起疾病的基因。
机译:内毒素治疗常染色体显性听力丧失体内传递基因组编辑剂
机译:在外毛细胞的体内基因编辑防止逐步的kcnq4鼠模型中的逐步听力损失
机译:在常染色体显性多囊肾病小鼠模型中体内诱导体细胞pkd1突变。