首页>
外国专利>
CHEMICALLY MODIFIED GUIDE RNAS FOR GENOME EDITING WITH CAS9
CHEMICALLY MODIFIED GUIDE RNAS FOR GENOME EDITING WITH CAS9
展开▼
机译:用CAS9进行化学修饰的导向RNA
展开▼
页面导航
摘要
著录项
相似文献
摘要
Provided herein are compositions for gene modification or editing and methods of using same to treat or prevent certain conditions. Specific compositions and methods capable of safely and effectively editing gene targets expressed in the liver to durably lower LDL-C thereby treating a leading cause of cardiovascular disease are disclosed.
展开▼