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ALLELE-SPECIFIC SILENCING OF TRANSFORMING GROWTH FACTOR BETA INDUCED GENE WITH R124H MUTATION USING SHORT INTERFERING RNA
ALLELE-SPECIFIC SILENCING OF TRANSFORMING GROWTH FACTOR BETA INDUCED GENE WITH R124H MUTATION USING SHORT INTERFERING RNA
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机译:用短干扰RNA使用R 12 4 H突变转化生长因子β诱导基因的等位基因特异性沉默
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摘要
The present disclosure relates to a ribonucleic acid (RNA) complex and methods of use thereof for preventing, ameliorating or treating symptoms associated with granular corneal dystrophy type 2 in a subject.
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