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ANTI-SICKLING BETA-GLOBIN PROTEIN, COMPOSITIONS AND METHODS FOR TREATING SICKLE CELL DISEASE
ANTI-SICKLING BETA-GLOBIN PROTEIN, COMPOSITIONS AND METHODS FOR TREATING SICKLE CELL DISEASE
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机译:抗-β-球蛋白蛋白,组成和治疗S病的方法
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摘要
Gene therapy methods and compositions for high level expression of anti-sickling globin proteins in erythroid cells for treating Sickle Cell disease are described.
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