首页> 外国专利> GENETIC AND PROTEIN THERAPY PRODUCTS FOR TREATING CYSTIC FIBROSIS AND INDUCING A GLUTATHIONE-S-TRANSFERASE FUNCTION

GENETIC AND PROTEIN THERAPY PRODUCTS FOR TREATING CYSTIC FIBROSIS AND INDUCING A GLUTATHIONE-S-TRANSFERASE FUNCTION

机译:用于治疗囊性纤维化和诱导谷胱甘肽-S-转移酶功能的基因和蛋白质治疗产品

摘要

The invention concerns a DNA molecule containing a DNA sequence whereof the expression product has a common peptide sequence with part of that of CFTR, in particular the one extending from the 430th to the 660th residue of the latter and having a glutathione carrier function. Said DNA molecule is useful for constructing vectors useful in gene therapy for treating cystic fibrosis.
机译:本发明涉及一种DNA分子,该DNA分子包含其表达产物具有与CFTR的一部分相同的肽序列的DNA序列,特别是从CFTR的430th至660th残基延伸并具有CFTR的DNA序列。谷胱甘肽载体功能。所述DNA分子可用于构建可用于治疗囊性纤维化的基因治疗的载体。

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