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Adeno-associated viral vector-mediated expression of factor VIII activity
Adeno-associated viral vector-mediated expression of factor VIII activity
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机译:腺相关病毒载体介导的因子VIII活性表达
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摘要
The instant invention provides methods and materials for expressing polypeptides with factor VIII activity comprising administering at least two rAAV vectors encoding different domains of human factor VIII and at least the heavy and light chains.
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