首页> 外国专利> USE OF LONG-CHAIN N-ALKYL DERIVATIVES OF DEOXYNOJIRIMYCIN FOR THE MANUFACTURE OF A MEDICAMENT FOR THE TREATMENT OF GLYCOLIPID STORAGE DISEASES

USE OF LONG-CHAIN N-ALKYL DERIVATIVES OF DEOXYNOJIRIMYCIN FOR THE MANUFACTURE OF A MEDICAMENT FOR THE TREATMENT OF GLYCOLIPID STORAGE DISEASES

机译:脱氧吉利霉素长链N-烷基衍生物在制备治疗糖脂贮积病的药物中的应用

摘要

A novel method is disclosed for the treatment of a patient affected withGaucher's disease or other such glycolipid storage diseases. Themethod comprises administering to said patient a therapeutically effectiveamount of a long-chain N-alkyl derivative of deoxynojirimycinto alleviate or inhibit the glycolipid storage disease. The long-chain alkylgroup has from nine to about 20 carbon atoms and preferably isnonyl or decyl.
机译:公开了一种新颖的方法来治疗受感染的患者高雪氏病或其他此类糖脂贮积病。的该方法包括对所述患者给予治疗有效脱氧野rim霉素的长链N-烷基衍生物的量减轻或抑制糖脂贮积病。长链烷基该基团具有9至约20个碳原子,优选为壬基或癸基。

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