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DRUGS COMPRISING AT INHIBITOR OF CLASS I ALPHA MANNOSIDASE FOR THE TREATMENT OF SARCOGLYCANOPATHIES
DRUGS COMPRISING AT INHIBITOR OF CLASS I ALPHA MANNOSIDASE FOR THE TREATMENT OF SARCOGLYCANOPATHIES
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机译:包含I类α甘露糖苷酶抑制剂的药物用于治疗糖皮质激素病
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摘要
Inhibitors of the endoplasmic reticulum associated degradation (ERAD) pathway, particularly inhibitors of mannosidase I, are used to treat sarcoglycanopathies.
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