首页> 外国专利> TAIL VARIANT OF OXIDATION-REDUCTION ACTIVITY THERAPEUTIC AGENT FOR THERAPY OF MITOCHONDRIAL DISEASE AND RELATED CONDITION AND FOR ADJUSTMENT OF ENERGY BIOMARKER

TAIL VARIANT OF OXIDATION-REDUCTION ACTIVITY THERAPEUTIC AGENT FOR THERAPY OF MITOCHONDRIAL DISEASE AND RELATED CONDITION AND FOR ADJUSTMENT OF ENERGY BIOMARKER

机译:用于治疗线粒体疾病和相关状况以及调节能量生物标志物的氧化还原活性治疗剂的尾部变量

摘要

PROBLEM TO BE SOLVED: To provide a compound useful for therapy or suppression of diseases due to mitochondrial diseases and for adjustment of an energy biomarker in a subject.SOLUTION: A method of treating a mitochondrial disease, adjusting 1 or more energy biomarkers, normalizing 1 or more energy biomarkers, or enhancing 1 or more energy biomarkers comprises a step of administering a therapeutically effective amount of a hydroquinone compound represented by the formula or an oxidized form thereof (a quinone compound) to a subject (Rto Rare each independently a C1 to 4 alkyl or the like; and Ris a C1 to 20 alkyl, alkenyl or the like.)
机译:解决的问题:提供一种化合物,该化合物可用于治疗或抑制线粒体疾病所致疾病以及调节受试者体内的能量生物标志物。解决方案:一种治疗线粒体疾病的方法,调节一种或多种能量生物标志物,将1归一化一种或多种能量生物标记,或增强一种或多种能量生物标记,包括以下步骤:将治疗有效量的下式表示的氢醌化合物或其氧化形式(醌化合物)施用于受试者(Rto Rare各自独立地为C1至4个烷基等; R 1为碳数1〜20的烷基,烯基等。

著录项

  • 公开/公告号JP2015078224A

    专利类型

  • 公开/公告日2015-04-23

    原文格式PDF

  • 申请/专利权人 EDISON PHARMACEUTICALS INC;

    申请/专利号JP20140254928

  • 发明设计人 MILLER GUY M;HECHT SIDNEY M;

    申请日2014-12-17

  • 分类号A61K31/05;A61P43;A61P25/08;A61P25/28;A61P25;A61P9;A61P25/16;A61P21/02;A61P25/14;A61P25/22;A61P25/18;A61P25/24;A61P15/12;A61P27/02;A61P3/10;A61P35;A61K31/122;C07C39/08;C07C50/02;C07C50/06;

  • 国家 JP

  • 入库时间 2022-08-21 15:33:40

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