APPLICATION OF GSK3 INHIBITOR IN PREPARING A DRUG TO TREAT NIEMANN-PICK DISEASE TYPE C

摘要

An application of a GSK3 inhibitor in preparation of a drug for treating Niemann-Pick disease type C. The GSK3 inhibitor can significantly improve the self-renewal and differentiation capacities of NPC1 KD or NPC1 KO hematopoietic and neural stem cells.