TREATMENT OF PATIENTS WITH CLASSIC FABRY DISEASE

摘要

Provided are methods for the treatment of classic Fabry disease in a patient. Certain methods comprise administering to the patient about 123 mg free base equivalent of migalastat for reducing kidney globotriaosylceramide, stabilizing renal function, reducing left ventricular mass, reducing plasma globotriaosylsphingosine and/or treating gastrointestinal symptoms.