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17β-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

机译:17β-羟基类固醇脱氢酶13型(HSD17B13)iRNA组成及其使用方法

摘要

The invention relates to double-stranded ribonucleic acid (dsRNA) compositions targeting the HSD17B 13 gene, as well as methods of inhibiting epression of HSD17B13, and methods of treating subjects that would benefit from reduction in expression of HSD17B13, such as subjects having a HSD17B13-associated disease, disorder, or condition, using such dsRNA compositions.
机译:本发明涉及靶向HSD17B 13基因的双链核糖核酸(dsRNA)组合物,以及抑制HSD17B13表达的方法,以及治疗受益于HSD17B13表达降低的受试者的方法,例如患有HSD17B13的受试者。 -使用此类dsRNA组合物的相关疾病,病症或病状。

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