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GLOBAL ORGANISATION OF RNA WITH IMPROVED CHARACTERISTICS FOR THE DETERMINATION OF NETHERLANDS
GLOBAL ORGANISATION OF RNA WITH IMPROVED CHARACTERISTICS FOR THE DETERMINATION OF NETHERLANDS
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机译:具有改进特性的RNA的全球组织,用于荷兰的测定
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摘要
This invention provides improved oligonucleotide and its use for therapeutic treatment,improvement,prevention,delay and/or therapeutic management of a genetic neuromuscular or neurodegenerative disorder related to human cis-component recurrent instability.
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