Combined therapy for Duchenne muscular dystrophy

摘要

An isolated antisense oligonucleotide (AON) capable of inducing exon skipping in a dystrophin pre-mRNA, for use in the treatment of Duchenne muscular dystrophy in combination with a viral vector encoding a Duchenne muscular dystrophy therapeutic , wherein said treatment comprises administering said oligonucleotide before administering said viral vector.