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PROGRAMMABLE DESIGNER THERAPEUTIC FUSOGENIC SECRETED GECTOSOME VESICLES FOR MACROMOLECULE DELIVERY AND GENOME MODIFICATION
PROGRAMMABLE DESIGNER THERAPEUTIC FUSOGENIC SECRETED GECTOSOME VESICLES FOR MACROMOLECULE DELIVERY AND GENOME MODIFICATION
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机译:用于大分子传递和基因组修饰的可编程设计的治疗性,遗传性分泌型核糖体囊泡
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摘要
The invention includes systems, methods, and compositions for designing secreted fusogenic ectosome vesicles, or gectosomes, that selectively encapsulate specific target proteins, nucleic acids and/or other small molecules in a predetermined manner. These engineered gectosomes can be used to deliver desired cargos to receipt cells in vitro, ex vivo, or in vivo and may further reprogram target cellular phenotypes in a dose-dependent manner, as well as perform genome editing functions among others.
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