机译:纠正人类胚胎中的致病基因突变
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Inst for Basic Sci Korea, Ctr Genome Engn, 70 Yuseong Daero 1689 Gil, Daejeon 34047, South Korea;
Salk Inst Biol Studies, Gene Express Lab, 10010 North Torrey Pines Rd, La Jolla, CA 92037 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Salk Inst Biol Studies, Gene Express Lab, 10010 North Torrey Pines Rd, La Jolla, CA 92037 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Inst for Basic Sci Korea, Ctr Genome Engn, 70 Yuseong Daero 1689 Gil, Daejeon 34047, South Korea;
Seoul Natl Univ, Dept Chem, 599 Gwanak Ro, Seoul 151747, South Korea;
Inst for Basic Sci Korea, Ctr Genome Engn, 70 Yuseong Daero 1689 Gil, Daejeon 34047, South Korea;
BGI Shenzhen, Bldg 11, Shenzhen 518083, Peoples R China|BGI Shenzhen, China Natl GeneBank, Jinsha Rd, Shenzhen 518210, Peoples R China|BGI Qingdao, 2877 Tuanjie Rd,Sino German Ecopk, Qingdao 266000, Peoples R China|BGI Shenzhen, Shenzhen Engn Lab Innovat Mol Diagnost, Bldg 11, Shenzhen 518083, Peoples R China;
BGI Shenzhen, Bldg 11, Shenzhen 518083, Peoples R China|BGI Shenzhen, China Natl GeneBank, Jinsha Rd, Shenzhen 518210, Peoples R China|BGI Qingdao, 2877 Tuanjie Rd,Sino German Ecopk, Qingdao 266000, Peoples R China;
BGI Shenzhen, Bldg 11, Shenzhen 518083, Peoples R China|BGI Shenzhen, China Natl GeneBank, Jinsha Rd, Shenzhen 518210, Peoples R China|BGI Qingdao, 2877 Tuanjie Rd,Sino German Ecopk, Qingdao 266000, Peoples R China;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA|Oregon Hlth & Sci Univ, Dept Obstet & Gynecol, Div Reprod Endocrinol & Infertil, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Dept Obstet & Gynecol, Div Reprod Endocrinol & Infertil, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Dept Obstet & Gynecol, Div Reprod Endocrinol & Infertil, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Dept Obstet & Gynecol, Div Reprod Endocrinol & Infertil, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Knight Cardiovasc Inst, 3181 Southwest,Sam Jackson Pk Rd, Portland, OR 97239 USA;
Salk Inst Biol Studies, Gene Express Lab, 10010 North Torrey Pines Rd, La Jolla, CA 92037 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA|Oregon Hlth & Sci Univ, Dept Obstet & Gynecol, Div Reprod Endocrinol & Infertil, 3303 Southwest,Bond Ave, Portland, OR 97239 USA;
Inst for Basic Sci Korea, Ctr Genome Engn, 70 Yuseong Daero 1689 Gil, Daejeon 34047, South Korea|Seoul Natl Univ, Dept Chem, 599 Gwanak Ro, Seoul 151747, South Korea;
Oregon Hlth & Sci Univ, Knight Cardiovasc Inst, 3181 Southwest,Sam Jackson Pk Rd, Portland, OR 97239 USA;
Oregon Hlth & Sci Univ, Ctr Embryon Cell & Gene Therapy, 3303 Southwest,Bond Ave, Portland, OR 97239 USA|Oregon Hlth & Sci Univ, Knight Cardiovasc Inst, 3181 Southwest,Sam Jackson Pk Rd, Portland, OR 97239 USA;
机译:Re:纠正人胚胎中的致病基因突变
机译:人体胚胎基因编辑以正确致病基因突变的突破
机译:基础编辑在人细胞和杂合胚中校正马法综合征致病性FBN1突变
机译:在人体线粒体病变中确定ATP酶6的致病与非致病性突变的进化分析
机译:调查导致常染色体显性遗传性视网膜色素变性的两个普遍表达的管家基因突变的致病性。
机译:通过人类细胞和杂合子胚胎的碱基编辑对马凡氏综合征病原性FBN1突变的校正。
机译:更正:致病性LRRK2突变不会改变细胞模型系统或人脑组织中的基因表达