机译:肝脏中多重基因编辑的多功能非血流输送系统
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA;
Columbia Univ Dept Biomed Engn New York NY 10027 USA|Sun Yat Sen Univ Lab Biomat & Translat Med Affiliated Hosp 3 Guangzhou 510630 Peoples R China;
Columbia Univ Dept Biomed Engn New York NY 10027 USA|South China Univ Technol Inst Life Sci Sch Biomed Sci & Engn Guangzhou 510006 Guangdong Peoples R China|South China Univ Technol Natl Engn Res Ctr Tissue Restorat & Reconstruct Guangzhou 510006 Guangdong Peoples R China;
Columbia Univ Dept Biomed Engn New York NY 10027 USA|Columbia Univ Dept Syst Biol Med Ctr New York NY 10032 USA;
cardiovascular disease; CRISPR; Cas9; gene therapy; multiplex gene editing; nanoparticles;
机译:使用Lentiflash(R)的一体化将基因编辑系统和体内递送到主要细胞和体内的MS2-嵌合病毒RNA递送工具,专为临床应用而设计
机译:使用非血管向量的递送系统递送mRNA治疗剂的纳米技术
机译:用于基因传递的病毒和非病毒传递系统
机译:斑马鱼心脏中基于纳米颗粒的siRNA的非病毒传递:基因沉默效率和siRNA生物分布。
机译:了解体内基因传递的障碍并开发非病毒载体以实现更有效的基因传递。
机译:基于CRISPR / CAS的基因编辑系统提供慢病毒载体:当前状态和观点
机译:用于基因递送的病毒和非病毒递送系统