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THERAPEUTIC GENE EDITING FOR ELANE-ASSOCIATED DISEASE
THERAPEUTIC GENE EDITING FOR ELANE-ASSOCIATED DISEASE
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机译:Elane相关疾病治疗基因编辑
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摘要
Provided herein are reagents and methods for targeting the ELANE gene for inhibition. Further provided herein is a method for producing a progenitor cell or a population of progenitor cells having decreased ELANE mRNA or protein expression.
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