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METHODS FOR TREATING PATIENTS HAVING CFH MUTATIONS WITH RECOMBINANT CFH PROTEINS

机译:用重组CFH蛋白治疗具有CFH突变的患者的方法

摘要

The present disclosure provides methods for treating, preventing, or inhibiting diseases in patients having one or more mutations in complement factor H (CFH), complement component 3 (C3), and complement factor B (CFB). Also provided are combination therapies comprising a CFH protein and a VEGF antagonist for treating neovascularization-associated ocular diseases.
机译:本公开提供了用于治疗,预防或抑制具有互补因子H(CFH),补体组分3(C3)和补体因子B(CFB)中具有一个或多个突变的患者的患者的疾病的方法。还提供了包含CFH蛋白和VEGF拮抗剂的组合疗法,用于治疗新生血管相关的眼部疾病。

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