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MATERIALS AND METHODS FOR THE TREATMENT OF DISORDERS ASSOCIATED MUTATIONS IN THE IRF2BPL GENE
MATERIALS AND METHODS FOR THE TREATMENT OF DISORDERS ASSOCIATED MUTATIONS IN THE IRF2BPL GENE
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机译:用于治疗IRF2BPL基因中疾病相关突变的材料和方法
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摘要
The disclosure provides gene therapy vectors, such as adeno-associated virus (AAV), designed for treatment of an Interferon regulatory factor 2 binding protein like (IRF2BPL) disorder.
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