Compositions and Methods for Inhibition of HAO1 (Hydroxy Oxidase 1 (Glycolic Acid Oxidase)) Gene Expression

摘要

The invention relates to RNAi agents, e.g., double-stranded RNAi agents, targeting the HAO1 gene, and methods of using such RNAi agents to inhibit expression of HAO1 and methods of treating subjects having, e.g., PH1.