Dinucleotides for treatment of achondroplasia, reduce presence of mutated receptor in chondrocytes that shows decrease of pathological effects

摘要

The dinucleotides reduce the presence of a mutated receptor in chondrocytes that shows a decrease of the pathological effects associated with the disease. The dinucleotides of formula (I) reduce the presence of a mutated receptor in chondrocytes that shows a decrease of the pathological effects associated with the disease. [variables not defined] [Image].