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THERAPEUTIC METHOD FOR PELIZAEUS-MERZBACHER DISEASE, AND THERAPEUTIC AGENT USED FOR THE SAME
THERAPEUTIC METHOD FOR PELIZAEUS-MERZBACHER DISEASE, AND THERAPEUTIC AGENT USED FOR THE SAME
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机译:腓肠肌-马茨巴赫病的治疗方法及其所用的治疗剂
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摘要
PROBLEM TO BE SOLVED: To provide a therapeutic method for Pelizaeus-Merzbacher disease and a therapeutic agent used for the therapeutic method.SOLUTION: A therapeutic agent for Pelizaeus-Merzbacher disease includes, as an active ingredient, an inhibitor, which is exemplified by following chemical formula, inhibits an Akt signal transduction system, or inhibits a kinase activity of a PI3K protein or an Akt protein.
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