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USE OF SOBETIROME IN THE TREATMENT OF X-LINKED ADRENOLENOLEUKODYSTROPHY
USE OF SOBETIROME IN THE TREATMENT OF X-LINKED ADRENOLENOLEUKODYSTROPHY
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机译:磺胺异丁酮在X线肾上腺髓质核素治疗中的应用
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摘要
Described herein is the use of sobetirome for the treatment of neurodegenerative disease involving demyelination or other abnormalities with oligodendrocyte function, including but not limited to X-linked adrenoleukodystrophy (X-ALD), multiple sclerosis, cerebral palsy, and other leukodystropies.
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