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COMPOSITIONS AND METHODS OF MODULATION OF EXPRESSION OF RECEPTOR OF FACTOR OF GROWTH FIBROBLAST 3 TYPE (FGFR3)

机译:调节成纤维细胞3型(FGFR3)因子受体表达的组合物和方法

摘要

Disclosed are oligonucleotides which target and hybridize to nucleic acid molecules encoding FGFR3, leading to reduced expression of FGFR3. Reduction in the aberrant expression of FGFR3 is beneficial for the treatment of certain medical disorders, such as achondroplasia.
机译:公开了靶向并与编码FGFR3的核酸分子杂交并导致FGFR3表达降低的寡核苷酸。减少FGFR3的异常表达对于某些疾病如软骨发育不全的治疗是有益的。

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