Therapeutic agents for neurodegenerative diseases, lysosomal storage disorders and neurodegenerative diseases associated with defects in lysosomal storage

• 1. 用于在溶酶体贮积症或糖原贮积病的治疗中使用的作为胞吐作用活化化合物的比卡鲁胺类似物或(S)-比卡鲁胺 [P] . 中国专利： CN105828811A . 2016-08-03
• 2. 用于治疗溶酶体贮积症和以溶酶体功能障碍为特征的病症的组合物和方法 [P] . 中国专利： CN109789316A . 2019-05-21
• 3. Therapeutic agents for neurodegenerative diseases, lysosomal storage disorders and neurodegenerative diseases associated with defects in lysosomal storage [P] . 英国专利： GB201706867D0 . 2017-06-14

  机译： 用于神经变性疾病，溶酶体贮积病和与溶酶体贮积缺陷相关的神经变性疾病的治疗剂

• 4. Therapeutic agents for neurodegenerative diseases, lysosomal storage disorders and neurodegenerative diseases associated with defects in lysosomal storage [P] . 英国专利： GB201705766D0 . 2017-05-24

  机译： 用于神经变性疾病，溶酶体贮积病和与溶酶体贮积缺陷相关的神经变性疾病的治疗剂

• 5. Therapeutic agents for neurodegenerative diseases, lysosomal storage disorders and neurodegenerative diseases associated with defects in lysosomal storage [P] . 英国专利： GB201613829D0 . 2016-09-28

  机译： 用于神经变性疾病，溶酶体贮积病和与溶酶体贮积缺陷相关的神经变性疾病的治疗剂

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• 2. Neurodegenerative diseases as proteinopathies-driven immune disorders [J] . Fausta Ciccocioppo, Sebastiano Miscia, Giuseppina Bologna, 中国神经再生研究（英文版） . 2020,第005期
• 3. Current and future therapeutic strategies for the treatment of retinal neurodegenerative diseases [J] . Victoria Maneu, Pedro Lax, Nicolás Cuenca 中国神经再生研究：英文版 . 2022,第001期
• 4. Human iPSC-Based Models for the Development of Therapeutics Targeting Neurodegenerative Lysosomal Storage Diseases [J] . Luciani Marco, Gritti Angela, Meneghini Vasco Frontiers in Molecular Biosciences . 2020,第6期
• 5. Misrouting of v-ATPase subunit V0a1 dysregulates lysosomal acidification in a neurodegenerative lysosomal storage disease model [J] . Maria B. Bagh, Shiyong Peng, Goutam Chandra, Nature Communications . 2017,第1期
• 6. Lipid Involvement in Neurodegenerative Diseases of the Motor System: Insights from Lysosomal Storage Diseases [J] . James C. Dodge Frontiers in Molecular Neuroscience . 2017,第2期
• 7. Developing a Lysosomal Panel for Biomarker Discovery in Neurodegenerative Diseases Using PRM [C] . Simon Sjodin, Gunnar Brinkmalm, Annika Ohrfelt, ASMS Conference on Mass Spectrometry and Allied Topics . 2016
• 8. Targeting intercellular adhesion molecule-1 to enhance delivery of therapeutic enzymes for treatment of lysosomal storage diseases [D] . Hsu, Janet 2014
• 9. Human iPSC-Based Models for the Development of Therapeutics Targeting Neurodegenerative Lysosomal Storage Diseases [O] . Marco Luciani, Angela Gritti, Vasco Meneghini 2020
• 10. Human iPSC-Based Models for the Development of Therapeutics Targeting Neurodegenerative Lysosomal Storage Diseases [O] . Marco Luciani, Angela Gritti, Vasco Meneghini 2020

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