A regimen comprising (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4-diol for the treatment and prevention of lysosomal disorders and degenerative disorders of the central nervous system

摘要

Dosage regimens and kits comprising (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4-diol for the treatment and / or prevention of lysosomal storage disorders (such as Gaucher disease) are described herein. Described in. (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4 for the treatment and / or prevention of degenerative disorders of the central nervous system (such as synucleinopathic Parkinson's disease or Lewy body dementia) -Dosing regimens and kits containing diols are also described. [Selection] Figure 1