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COMPOSITIONS ON THE BASIS OF IRNA FOR TRANSTYRETINE (TTR) AND METHODS OF THEIR APPLICATION FOR THE TREATMENT OR PREVENTION OF TTR ASSOCIATED DISTRIBUTIONS
COMPOSITIONS ON THE BASIS OF IRNA FOR TRANSTYRETINE (TTR) AND METHODS OF THEIR APPLICATION FOR THE TREATMENT OR PREVENTION OF TTR ASSOCIATED DISTRIBUTIONS
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机译:反式酪氨酸(TTR)的IRNA组成及其在治疗或预防TTR相关分布中的应用方法
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摘要
The present invention provides iRNA-based agents, for example, double-strand iRNA-based agents that target the transthyretin gene (TTR), and methods of using such iRNA-based agents to treat or prevent TTR-associated diseases.
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