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COMPOSITIONS ON THE BASIS OF IRNA FOR TRANSTYRETINE (TTR) AND METHODS OF THEIR APPLICATION FOR THE TREATMENT OR PREVENTION OF TTR ASSOCIATED DISTRIBUTIONS

机译:反式酪氨酸(TTR)的IRNA组成及其在治疗或预防TTR相关分布中的应用方法

摘要

The present invention provides iRNA-based agents, for example, double-strand iRNA-based agents that target the transthyretin gene (TTR), and methods of using such iRNA-based agents to treat or prevent TTR-associated diseases.
机译:本发明提供了基于iRNA的试剂,例如靶向运甲状腺素蛋白基因(TTR)的基于双链基于iRNA的试剂,以及使用这种基于iRNA的试剂来治疗或预防与TTR相关的疾病的方法。

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