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ADENO-ASSOCIATED VIRAL VECTORS FOR GENE THERAPY

机译:用于基因治疗的腺相关病毒载体

摘要

Genetically modified compositions, such as adeno-associated viral vectors and primary cells, for treating various conditions and diseases. Disclosed are also modified adeno-associated viruses for the treatment of cancer. Also disclosed are the methods of making and using the genetically modified compositions in treating various diseases, conditions, and cancer.
机译:基因修饰的组合物,例如腺相关病毒载体和原代细胞,用于治疗各种疾病和疾病。还公开了用于治疗癌症的修饰的腺相关病毒。还公开了制备和使用遗传修饰的组合物来治疗各种疾病,病症和癌症的方法。

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