READTHROUGH INDUCER AND PHARMACEUTICAL USE THEREOF

摘要

The present invention pertains to a compound represented by general formula (I) [the symbols in the formula are as described in the specification] or a pharmacologically acceptable salt thereof, and to a pharmaceutical composition containing said compound as an active ingredient. Because the abovementioned compound has readthrough activity, the present invention makes it possible to provide a medicine useful as an agent for the prevention or treatment of nonsense mutation-type genetic diseases such as mucopolysaccharidosis, muscular dystrophy, Duchenne muscular dystrophy, multiple sclerosis, cystic fibrosis, ceroid lipofuscinosis, and Neiman-Pick disease.