...
机译:丙酮酸激酶激活剂 mitapivat 可减少溶血并改善 β-地中海贫血小鼠模型中的贫血
Harvard Med Sch, Boston Childrens Hosp, Dept Lab Med, 300 Longwood Ave, Boston, MA 02115 USA;
Univ Napoli Federico II, Dipartimento Med Mol & Biotecnol Med, Naples, Italy;
Univ Verona, Dept Med, Verona, ItalyAgios Pharmaceut Inc, Cambridge, MA USAUniv Padua, Dept Women & Childrens Hlth, Clin Genet Unit, Padua, ItalyINSERM, Paris, FranceUniv Torino, Dept Oncol, Turin, ItalyUniv Calif Los Angeles, David Geffen Sch Med, Dept Med, Los Angeles, CA 90095 USA;
机译:Mitapivat sulfate Pyruvate kinase isozyme R activator Treatment of pyruvate kinase deficiency Treatment of thalassemia Treatment of sickle cell disease
机译:An evaluation of mitapivat for the treatment of hemolytic anemia in adults with pyruvate kinase deficiency
机译:Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in sickle cell disease: A phase 2, open‐label study