机译:Engineering a lysosomal enzyme with a derivative of receptor-binding domain of apoE enables delivery across the blood-brain barrier
Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45229, United States;
Division of Developmental Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45229, United States;
Department of Pathology, University of Cincinnati, Cincinnati, OH 45267, United StatesNational Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20892, United States;
CNS protein delivery; In vivo evaluation; LDL receptor-related protein 1; Lysosomal storage diseases; Neurological disorders;