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机译:成本效用Voretigene NeparvovecBiallelic RPE65-Mediated遗传性视网膜疾病
Univ Washington, Pharmaceut Outcomes Res & Policy Program, Dept Pharm, Seattle, WA 98195 USA;
Inst Clin & Econ Review, Boston, MA USA;
Health Care Systems; Retinal Diseases; Genetic TherapyPerspectivehealth economicsQuality-Adjusted Life YearsBlindnessMentoring;
机译:视网膜下后Perifoveal视网膜脉络膜萎缩Voretigene Neparvovec-rzyl for RPE65-Mediated雷伯氏先天性黑内障
机译:voretigene neparvovec(Luxturna°)和某些形式的遗传视网膜营养不良
机译:voretigene neparvovec和Leber先天性阿瓜症的基因治疗:迄今为止审查证据
机译:voretigene neparvovec的耐久性Biallelic RPE65介导的遗传性视网膜疾病