THERAPEUTIC AGENT FOR DUCHENNE MUSCULAR DYSTROPHY

摘要

PROBLEM TO BE SOLVED: To provide a measure for therapy of Duchenne muscular dystrophy by inducing skipping of dystrophine exon 45.;SOLUTION: Disclosed are an anti-sense oligonucleotide comprising a base sequence complementary to a sequence represented by a specific base sequence derived from a human dystrophine and a therapeutic agent for Duchenne muscular dystrophy comprising the same.;COPYRIGHT: (C)2003,JPO