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GLYCOLIPID METABOLIC ABNORMALITY TREATING AGENT

机译:糖脂代谢异常治疗剂

摘要

PROBLEM TO BE SOLVED: To provide a glycolipid metabolic abnormality treating agent useful to glycolipid metabolic abnormality caused by human &bgr;-galactosidase gene mutations.SOLUTION: The invention provides a treating agent of glycolipid metabolic abnormality caused by &bgr;-galactosidase gene mutations which contains as an active ingredient a conduramine F-4 derivative represented by the formula (1) or a pharmaceutically acceptable salt thereof. (Rand Rare each independently H or an alkyl group, an alkenyl group, an alkynyl group, and an acyl group and the like; Rto Rare each independently a hydroxyl group having a substituent selected from a hydroxyl group or an alkyl group, an acyl group, a silyl group, an aralkyl group, an alkoxyalkyl group, and an aralkyloxy alkyl group.)
机译:解决的问题:提供一种糖脂代谢异常治疗剂,其可用于由人β-半乳糖苷酶基因突变引起的糖脂代谢异常。解决方案:本发明提供一种由β-半乳糖苷酶基因突变引起的糖脂代谢异常的治疗剂,其包含作为活性成分,由式(1)表示的conduramine F-4衍生物或其药学上可接受的盐。 (RandR各自独立地为H或烷基,烯基,炔基和酰基等; RtoR各自独立地为具有选自羟基或烷基,酰基的取代基的羟基。 ,甲硅烷基,芳烷基,烷氧基烷基和芳烷氧基烷基。)

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