TREATMENT OF HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA.

摘要

(R)-2-(4-((2-Ethoxy-3-(4-(trifluoromethyl)phenoxy)propyl)thio)-2 -methylphenoxy)- acetic acid or a salt thereof; optionally in combination with an MTP inhibitor, an apoB- 100 synthesis inhibitor, or a PCSK9 inhibitor; is useful in the treatment of homozygous familial hypercholesterolemia.