首页> 外国专利> B CELLS GENETICALLY ENGINEERED TO SECRETE FOLLISTATIN AND METHODS OF USING THE SAME TO TREAT FOLLISTATIN-RELATED DISEASES, CONDITIONS, DISORDERS AND TO ENHANCE MUSCLE GROWTH AND STRENGTH

B CELLS GENETICALLY ENGINEERED TO SECRETE FOLLISTATIN AND METHODS OF USING THE SAME TO TREAT FOLLISTATIN-RELATED DISEASES, CONDITIONS, DISORDERS AND TO ENHANCE MUSCLE GROWTH AND STRENGTH

机译:遗传性用于分泌福斯特菌素的B细胞及其使用方法治疗与福斯特菌素相关的疾病,病症,疾病和增强肌肉生长和强度

摘要

The present invention relates to methods for administering autologous and/or allogeneic B cells genetically modified to produce a therapeutic agent, such as follistatin. Specifically disclosed are methods for administering a single, maximally effective dose of genetically modified B cells and for administering multiple doses of genetically modified B cells that express follistatin. The compositions and methods disclosed herein are useful for the long-term, in vivo delivery of follistatin.
机译:本发明涉及施用经基因修饰以产生治疗剂例如卵泡抑素的自体和/或同种异体B细胞的方法。具体公开了用于给予单个最大有效剂量的基因修饰的B细胞和用于给予多剂量表达卵泡抑素的基因修饰的B细胞的方法。本文公开的组合物和方法可用于卵泡抑素的长期体内递送。

著录项

  • 公开/公告号WO2019178613A1

    专利类型

  • 公开/公告日2019-09-19

    原文格式PDF

  • 申请/专利权人 IMMUSOFT CORPORATION;

    申请/专利号WO2019US22821

  • 申请日2019-03-18

  • 分类号C12N5/0781;C07K14/47;A61K35/17;A61P21;C12N15/64;

  • 国家 WO

  • 入库时间 2022-08-21 11:53:09

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