...
机译:Patient selection may affect gene therapy success. Dominant negative effects observed for ornithine transcarbamylase in mouse and human hepatocytes.
Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas 77030, USA.;
Gene Therapy; Metabolism; Inborn Errors; Ornithine Carbamoyltransferase; 基因疗法; 代谢缺陷; 先天性; 鸟氨酸氨甲酰转移酶; 病人选择;