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机译:Ethylenedioxy-PIP2 oxalate reduces ganglioside storage in juvenile sandhoff disease mice
Boston College Biology Department, Chestnut Hill, MA 02467, United States;
Department of Medicinal Chemistry, College of Pharmacy, University of Michigan, Ann Arbor, MI 48109;
Ganglioside; Glycosphingolipid; Lysosomal storage disease; Neurodegeneration; Sandhoff disease; Substrate reduction therapy;